Editorial: Ex-vivo and in-vivo genome engineering for metabolic and neurometabolic diseases

oleh: Pasqualina Colella, Vasco Meneghini, Vasco Meneghini, Guilherme Baldo, Natalia Gomez-Ospina

Format: Article
Diterbitkan: Frontiers Media S.A. 2023-07-01

Deskripsi

Subjek

genome editing; neurometabolic; liver; retina; HSPC; metabolic