Meaningful changes in motor function in Duchenne muscular dystrophy (DMD): A multi-center study

oleh: Francesco Muntoni, James Signorovitch, Gautam Sajeev, Nicolae Done, Zhiwen Yao, Nathalie Goemans, Craig McDonald, Eugenio Mercuri, Erik H. Niks, Brenda Wong, Krista Vandenborne, Volker Straub, Imelda J. M. de Groot, Cuixia Tian, Adnan Manzur, Ibrahima Dieye, Henry Lane, Susan J. Ward, Laurent Servais

Format: Article
Diterbitkan: Public Library of Science (PLoS) 2024-01-01

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