O30: REKLAIM: A first in human phase Ib clinical trial of FBX-101 (AAVrh10.GALC) intravenously administered after UCBT for infantile Krabbe disease

oleh: Maria Escolar, Mark Vander Lugt, Raymond Wang, Juan Ruiz, Michele Poe, Paul Szabolcs

Format: Article
Diterbitkan: Elsevier 2024-01-01

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