P171: Developing an approach to screening rare genetic diagnoses for amenability to bespoke genetic therapy development

oleh: David Cheerie, Marlen Lauffer, Danique Beijer, Matthis Synofzik, Annemieke Aartsma-Rus, Michael Szego, Kimberly Amburgey, Brian Kalish, James Dowling, Gregory Costain

Format: Article
Diterbitkan: Elsevier 2024-01-01

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