Elivaldogene autotemcel approved for treatment of cerebral adrenoleukodystrophy (CALD) in males: A therapeutics bulletin of the American College of Medical Genetics and Genomics (ACMG)
oleh: Anna I. Scott, Kanwaldeep K. Mallhi, Jaya Ganesh, Wei-Liang Chen
| Format: | Article |
|---|---|
| Diterbitkan: | Elsevier 2023-01-01 |
Deskripsi
Subjek
Cerebral; Elivaldogene; Gene therapy; Newborn screening; X-linked adrenoleukodystrophy