P1453: STABLE TRANSDUCTION OF FETAL HEMOGLOBIN IN PATIENTS WITH SICKLE CELL DISEASE IN THE PHASE 1/2 MOMENTUM STUDY OF ARU-1801 GENE THERAPY AND REDUCED INTENSITY CONDITIONING

oleh: M. Grimley, M. Kent, M. Asnani, A. Shrestha, S. Felker, C. Lutzko, P. Arumugam, S. Witting, J. Knight-Madden, O. Niss, C. Quinn, C. Lo, C. Little, A. Dong, P. Malik

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Diterbitkan: Wiley 2022-06-01

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