Corrigendum: Off-Label Use of Ataluren in Four Non-ambulatory Patients With Duchenne Muscular Dystrophy: Effects on Cardiac and Pulmonary Function and Muscle Strength
oleh: Daniel Ebrahimi-Fakhari, Ulrich Dillmann, Marina Flotats-Bastardas, Martin Poryo, Hashim Abdul-Khaliq, Mohammed Ghiath Shamdeen, Bernhard Mischo, Michael Zemlin, Sascha Meyer
| Format: | Article |
|---|---|
| Diterbitkan: | Frontiers Media S.A. 2019-07-01 |
Deskripsi
Subjek
Translarna; Duchenne muscular dystrophy; DMD; non-ambulatory; nmDMD; stop codon read-through therapy