O19: Integrated analyses of data from clinical trials of delandistrogene moxeparvovec gene therapy in DMD*

oleh: Erin O’Rourke, Crystal Proud, Craig Zaidman, Perry B. Shieh, Craig McDonald, John W. Day, Stefanie Mason, Maitea Guridi, Lixin Han, Lixi Yu, Carol Reid, Eddie Darton, Christoph Wandel, James Richardson, Jyoti Malhotra, Teji Singh, Louise Rodino-Klapac, Jerry Mendell

Format: Article
Diterbitkan: Elsevier 2023-01-01

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