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DEVELOPMENT OF THE ACCURATE SPINOCEREBELLAR ATAXIA TYPE3 (SCA3) THERAPEUTICS USING EN-CAS12A NICKASE-BASED GENOME EDITING
oleh: Lee Wha Gwon, Junghyung Park, Jinyoung Won, Jae-Won Huh, Youngjeon Lee, Seung Hwan Lee
Format: | Article |
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Diterbitkan: | Elsevier 2023-10-01 |
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