Hasil Pencarian - Simone Merlin
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1
Escape or Fight: Inhibitors in Hemophilia A oleh Simone Merlin, Simone Merlin, Antonia Follenzi, Antonia Follenzi
Diterbitkan 2020-03-01Dapatkan teks lengkap
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2
Transcriptional Targeting and MicroRNA Regulation of Lentiviral Vectors oleh Simone Merlin, Antonia Follenzi
Diterbitkan 2019-03-01Dapatkan teks lengkap
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Immune tolerance promotion by LSEC-specific lentiviral vector-mediated expression of the transgene regulated by the stabilin-2 promoter oleh Ester Borroni, Chiara Borsotti, Roberta A. Cirsmaru, Vakhtang Kalandadze, Rosella Famà, Simone Merlin, Brian Brown, Antonia Follenzi
Diterbitkan 2024-03-01Dapatkan teks lengkap
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5
Regulatory-Compliant Validation of a Highly Sensitive qPCR for Biodistribution Assessment of Hemophilia A Patient Cells oleh Patrick Bittorf, Thorsten Bergmann, Simone Merlin, Cristina Olgasi, Oliver Pullig, Ralf Sanzenbacher, Martin Zierau, Heike Walles, Antonia Follenzi, Joris Braspenning
Diterbitkan 2020-09-01Dapatkan teks lengkap
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6
Factor VIII promotes angiogenesis and vessel stability regulating extracellular matrix proteins oleh Cristina Olgasi, Alessia Cucci, Ivan Molineris, Simone Assanelli, Francesca Anselmi, Chiara Borsotti, Chiara Sgromo, Andrea Lauria, Simone Merlin, Gillian E. Walker, Salvatore Oliviero, Antonia Follenzi
Diterbitkan 2024-06-01Dapatkan teks lengkap
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7
Extrahepatic sources of factor VIII potentially contribute to the coagulation cascade correcting the bleeding phenotype of mice with hemophilia A oleh Diego Zanolini, Simone Merlin, Maria Feola, Gabriella Ranaldo, Angela Amoruso, Gianluca Gaidano, Mauro Zaffaroni, Alessandro Ferrero, Sandra Brunelleschi, Guido Valente, Sanjeev Gupta, Maria Prat, Antonia Follenzi
Diterbitkan 2015-07-01Dapatkan teks lengkap
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8
Liver gene therapy with intein‐mediated F8 trans‐splicing corrects mouse haemophilia A oleh Federica Esposito, Hristiana Lyubenova, Patrizia Tornabene, Stefano Auricchio, Antonella Iuliano, Edoardo Nusco, Simone Merlin, Cristina Olgasi, Giorgia Manni, Marco Gargaro, Francesca Fallarino, Antonia Follenzi, Alberto Auricchio
Diterbitkan 2022-06-01Dapatkan teks lengkap
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9
Activity and High-Order Effective Connectivity Alterations in Sanfilippo C Patient-Specific Neuronal Networks oleh Isaac Canals, Jordi Soriano, Javier G. Orlandi, Roger Torrent, Yvonne Richaud-Patin, Senda Jiménez-Delgado, Simone Merlin, Antonia Follenzi, Antonella Consiglio, Lluïsa Vilageliu, Daniel Grinberg, Angel Raya
Diterbitkan 2015-10-01Dapatkan teks lengkap
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10
Therapeutic potential of fetal liver cell transplantation in hemophilia A mice oleh Simone Merlin, Saicharan Akula, Alessia Cottonaro, Tamara Garcia-Leal, Luis Javier Serrano, Ester Borroni, Vakhtang Kalandadze, Rocio Galiano, Chiara Borsotti, Antonio Liras, María José Sanchez, Antonia Follenzi
Diterbitkan 2023-01-01Dapatkan teks lengkap
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11
GP64-pseudotyped lentiviral vectors target liver endothelial cells and correct hemophilia A mice oleh Michela Milani, Cesare Canepari, Simone Assanelli, Simone Merlin, Ester Borroni, Francesco Starinieri, Mauro Biffi, Fabio Russo, Anna Fabiano, Desirèe Zambroni, Andrea Annoni, Luigi Naldini, Antonia Follenzi, Alessio Cantore
Diterbitkan 2024-04-01Dapatkan teks lengkap
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12
Deciphering the Ets-1/2-mediated transcriptional regulation of F8 gene identifies a minimal F8 promoter for hemophilia A gene therapy oleh Rosella Famà, Ester Borroni, Simone Merlin, Chiara Airoldi, Silvia Pignani, Alessia Cucci, Davide Corà, Valentina Bruscaggin, Sharon Scardellato, Stefania Faletti, Giuliana Pelicci, Mirko Pinotti, Gillian E. Walker, Antonia Follenzi
Diterbitkan 2020-05-01Dapatkan teks lengkap
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13
Human Cardiac Progenitor Spheroids Exhibit Enhanced Engraftment Potential. oleh Francesca Oltolina, Andrea Zamperone, Donato Colangelo, Luca Gregoletto, Simone Reano, Stefano Pietronave, Simone Merlin, Maria Talmon, Eugenio Novelli, Marco Diena, Carmine Nicoletti, Antonio Musarò, Nicoletta Filigheddu, Antonia Follenzi, Maria Prat
Diterbitkan 2015-01-01Dapatkan teks lengkap
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14
Correction: Human Cardiac Progenitor Spheroids Exhibit Enhanced Engraftment Potential. oleh Francesca Oltolina, Andrea Zamperone, Donato Colangelo, Luca Gregoletto, Simone Reano, Stefano Pietronave, Simone Merlin, Maria Talmon, Eugenio Novelli, Marco Diena, Carmine Nicoletti, Antonio Musarò, Nicoletta Filigheddu, Antonia Follenzi, Maria Prat
Diterbitkan 2015-01-01Dapatkan teks lengkap
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15
Patient-Specific iPSC-Derived Endothelial Cells Provide Long-Term Phenotypic Correction of Hemophilia A oleh Cristina Olgasi, Maria Talmon, Simone Merlin, Alessia Cucci, Yvonne Richaud-Patin, Gabriella Ranaldo, Donato Colangelo, Federica Di Scipio, Giovanni N. Berta, Chiara Borsotti, Federica Valeri, Francesco Faraldi, Maria Prat, Maria Messina, Piercarla Schinco, Angelo Lombardo, Angel Raya, Antonia Follenzi
Diterbitkan 2018-12-01Dapatkan teks lengkap
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16
Efficient and safe correction of hemophilia A by lentiviral vector-transduced BOECs in an implantable device oleh Cristina Olgasi, Chiara Borsotti, Simone Merlin, Thorsten Bergmann, Patrick Bittorf, Adeolu Badi Adewoye, Nicholas Wragg, Kelcey Patterson, Andrea Calabria, Fabrizio Benedicenti, Alessia Cucci, Alessandra Borchiellini, Berardino Pollio, Eugenio Montini, Delfina M. Mazzuca, Martin Zierau, Alexandra Stolzing, Philip.M. Toleikis, Joris Braspenning, Antonia Follenzi
Diterbitkan 2021-12-01Dapatkan teks lengkap
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