Hasil Pencarian - Rosario Mosca
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AAV-mediated gene therapy for galactosialidosis: A long-term safety and efficacy study oleh Huimin Hu, Rosario Mosca, Elida Gomero, Diantha van de Vlekkert, Yvan Campos, Leigh E. Fremuth, Scott A. Brown, Jason A. Weesner, Ida Annunziata, Alessandra d’Azzo
Diterbitkan 2021-12-01Dapatkan teks lengkap
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2
Galactosialidosis: preclinical enzyme replacement therapy in a mouse model of the disease, a proof of concept oleh Jaclyn Cadaoas, Huimin Hu, Gabrielle Boyle, Elida Gomero, Rosario Mosca, Kartika Jayashankar, Mike Machado, Sean Cullen, Belle Guzman, Diantha van de Vlekkert, Ida Annunziata, Michel Vellard, Emil Kakkis, Vish Koppaka, Alessandra d’Azzo
Diterbitkan 2021-03-01Dapatkan teks lengkap
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3
MYC competes with MiT/TFE in regulating lysosomal biogenesis and autophagy through an epigenetic rheostat oleh Ida Annunziata, Diantha van de Vlekkert, Elmar Wolf, David Finkelstein, Geoffrey Neale, Eda Machado, Rosario Mosca, Yvan Campos, Heather Tillman, Martine F. Roussel, Jason Andrew Weesner, Leigh Ellen Fremuth, Xiaohui Qiu, Min-Joon Han, Gerard C. Grosveld, Alessandra d’Azzo
Diterbitkan 2019-08-01Dapatkan teks lengkap
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