Hasil Pencarian - R Scott McIvor
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A Broad Range of Dose Optima Achieve High-level, Long-term Gene Expression After Hydrodynamic Delivery of Sleeping Beauty Transposons Using Hyperactive SB100x Transposase oleh Kelly M Podetz-Pedersen, Erik R Olson, Nikunj V Somia, Stephen J Russell, R Scott McIvor
Diterbitkan 2016-01-01Dapatkan teks lengkap
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Differences in MPS I and MPS II Disease Manifestations oleh Christiane S. Hampe, Brianna D. Yund, Paul J. Orchard, Troy C. Lund, Jacob Wesley, R. Scott McIvor
Diterbitkan 2021-07-01Dapatkan teks lengkap
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Direct gene transfer to the CNS prevents emergence of neurologic disease in a murine model of mucopolysaccharidosis type I oleh Daniel A. Wolf, Andrew W. Lenander, Zhenhong Nan, Lalitha R. Belur, Chester B. Whitley, Pankaj Gupta, Walter C. Low, R. Scott McIvor
Diterbitkan 2011-07-01Dapatkan teks lengkap
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Efficient Non-Viral Integration and Stable Gene Expression in Multipotent Adult Progenitor Cells oleh Andrew Wilber, Fernando Ulloa Montoya, Luke Hammer, Branden S. Moriarity, Aron M. Geurts, David A. Largaespada, Catherine M. Verfaillie, R. Scott McIvor, Uma Lakshmipathy
Diterbitkan 2011-01-01Dapatkan teks lengkap
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Intravenous delivery for treatment of mucopolysaccharidosis type I: A comparison of AAV serotypes 9 and rh10 oleh Lalitha R. Belur, Kelly M. Podetz-Pedersen, Thuy An Tran, Joshua A. Mesick, Nathaniel M. Singh, Maureen Riedl, Lucy Vulchanova, Karen F. Kozarsky, R. Scott McIvor
Diterbitkan 2020-09-01Dapatkan teks lengkap
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Non-invasive intravenous administration of AAV9 transducing iduronate sulfatase leads to global metabolic correction and prevention of neurologic deficits in a mouse model of Hunte... oleh Kanut Laoharawee, Kelly M. Podetz-Pedersen, Tam T. Nguyen, Sajya M. Singh, Miles C. Smith, Lalitha R. Belur, Walter C. Low, Karen F. Kozarsky, R. Scott McIvor
Diterbitkan 2023-03-01Dapatkan teks lengkap
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Mucopolysaccharidosis Type I: Current Treatments, Limitations, and Prospects for Improvement oleh Christiane S. Hampe, Jacob Wesley, Troy C. Lund, Paul J. Orchard, Lynda E. Polgreen, Julie B. Eisengart, Linda K. McLoon, Sebahattin Cureoglu, Patricia Schachern, R. Scott McIvor
Diterbitkan 2021-01-01Dapatkan teks lengkap
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Harnessing a high cargo-capacity transposon for genetic applications in vertebrates. oleh Darius Balciunas, Kirk J Wangensteen, Andrew Wilber, Jason Bell, Aron Geurts, Sridhar Sivasubbu, Xin Wang, Perry B Hackett, David A Largaespada, R Scott McIvor, Stephen C Ekker
Diterbitkan 2006-11-01Dapatkan teks lengkap
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Comparative dose effectiveness of intravenous and intrathecal AAV9.CB7.hIDS, RGX-121, in mucopolysaccharidosis type II mice oleh Miles C. Smith, Lalitha R. Belur, Andrea D. Karlen, Olivia Erlanson, Justin Furcich, Troy C. Lund, Davis Seelig, Kelley F. Kitto, Carolyn A. Fairbanks, Kwi Hye Kim, Nick Buss, R. Scott McIvor
Diterbitkan 2024-03-01Dapatkan teks lengkap
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Simple and efficient methods for enrichment and isolation of endonuclease modified cells. oleh Branden S Moriarity, Eric P Rahrmann, Dominic A Beckmann, Caitlin B Conboy, Adrienne L Watson, Daniel F Carlson, Erik R Olson, Kendra A Hyland, Scott C Fahrenkrug, R Scott McIvor, David A Largaespada
Diterbitkan 2014-01-01Dapatkan teks lengkap
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Supraspinal gene transfer by intrathecal adeno-associated virus serotype 5 oleh Daniel J. Schuster, Lalitha R. Belur, Maureen S. Riedl, Stephen A. Schnell, Kelly M. Podetz-Pedersen, Kelley F. Kitto, R. Scott McIvor, Lucy eVulchanova, Carolyn A. Fairbanks, Carolyn A. Fairbanks, Carolyn A. Fairbanks
Diterbitkan 2014-08-01Dapatkan teks lengkap
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AAV-mediated gene transfer to colon-innervating primary afferent neurons oleh Reshma Gore, Tina Esmail, Kelsey Pflepsen, Ezequiel Marron Fernandez de Velasco, Kelley F. Kitto, Maureen S. Riedl, Andrea Karlen, R. Scott McIvor, Christopher N. Honda, Carolyn A. Fairbanks, Carolyn A. Fairbanks, Carolyn A. Fairbanks, Lucy Vulchanova
Diterbitkan 2023-08-01Dapatkan teks lengkap
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Comparative Effectiveness of Intracerebroventricular, Intrathecal, and Intranasal Routes of AAV9 Vector Administration for Genetic Therapy of Neurologic Disease in Murine Mucopolys... oleh Lalitha R. Belur, Megan Romero, Junggu Lee, Kelly M. Podetz-Pedersen, Zhenhong Nan, Maureen S. Riedl, Lucy Vulchanova, Kelley F. Kitto, Carolyn A. Fairbanks, Karen F. Kozarsky, Paul J. Orchard, William H. Frey, Walter C. Low, R. Scott McIvor
Diterbitkan 2021-05-01Dapatkan teks lengkap
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Adeno-associated virus-mediated gene transfer of arginine decarboxylase to the central nervous system prevents opioid analgesic tolerance oleh Caroline C. Churchill, Cristina D. Peterson, Cristina D. Peterson, Cristina D. Peterson, Kelley F. Kitto, Kelsey R. Pflepsen, Lalitha R. Belur, R. Scott McIvor, Lucy Vulchanova, George L. Wilcox, George L. Wilcox, George L. Wilcox, Carolyn A. Fairbanks, Carolyn A. Fairbanks, Carolyn A. Fairbanks
Diterbitkan 2024-02-01Dapatkan teks lengkap
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Correction of Fanconi Anemia Mutations Using Digital Genome Engineering oleh Christopher J. Sipe, Mitchell G. Kluesner, Samuel P. Bingea, Walker S. Lahr, Aneesha A. Andrew, Minjing Wang, Anthony P. DeFeo, Timothy L. Hinkel, Kanut Laoharawee, John E. Wagner, Margaret L. MacMillan, Gregory M. Vercellotti, Jakub Tolar, Mark J. Osborn, R. Scott McIvor, Beau R. Webber, Branden S. Moriarity
Diterbitkan 2022-07-01Dapatkan teks lengkap
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333 Targeting the apical intracellular checkpoint CISH unleashes T cell neoantigen reactivity and effector program oleh Matthew Johnson, Ying Hu, Nicholas Restifo, Jared Gartner, Douglas Palmer, Shashank Patel, Maria Parkhurst, Todd Prickett, Parisa Malekzadeh, David McKenna, Zulmarie Franco, Suman Vodnala, Beau Webber, Yogin Patel, Christine Kariya, Walker Lahr, Rigel Kishton, Devikala Gurusamy, Miechaleen Diers, Natalie Wolf, Nicholas Slipek, Darin Sumstad, Lydia Viney, Tom Henley, Tilmann Bürckstümmer, Oliver Baker, Chunhua Yan, Daoud Meerzaman, Kartik Padhan, Winnie Lo, Li Jia, Drew Deniger, R Scott McIvor, Modassir Choudhry, Branden Moriarity
Diterbitkan 2020-11-01Artikel