Hasil Pencarian - Neelam Panchal
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Genome Editing With TALEN, CRISPR-Cas9 and CRISPR-Cas12a in Combination With AAV6 Homology Donor Restores T Cell Function for XLP oleh Benjamin C. Houghton, Neelam Panchal, Simone A. Haas, Simone A. Haas, Kay O. Chmielewski, Kay O. Chmielewski, Kay O. Chmielewski, Markus Hildenbeutel, Markus Hildenbeutel, Thomas Whittaker, Claudio Mussolino, Claudio Mussolino, Toni Cathomen, Toni Cathomen, Adrian J Thrasher, Claire Booth
Diterbitkan 2022-05-01
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Lentiviral Hematopoietic Stem Cell Gene Therapy Rescues Clinical Phenotypes in a Murine Model of Pompe Disease oleh Giuseppa Piras, Claudia Montiel-Equihua, Yee-Ka Agnes Chan, Slawomir Wantuch, Daniel Stuckey, Derek Burke, Helen Prunty, Rahul Phadke, Darren Chambers, Armando Partida-Gaytan, Diego Leon-Rico, Neelam Panchal, Kathryn Whitmore, Miguel Calero, Sara Benedetti, Giorgia Santilli, Adrian J. Thrasher, H. Bobby Gaspar
Diterbitkan 2020-09-01
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