Search Results - Nathalie Clément
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Manufacturing of recombinant adeno-associated viral vectors for clinical trials by Nathalie Clément, Joshua C Grieger
Published 2016-01-01
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Pharmacology of Recombinant Adeno-associated Virus Production by Magalie Penaud-Budloo, Achille François, Nathalie Clément, Eduard Ayuso
Published 2018-03-01
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The comparability tales: A phase-appropriate roadmap for CGT drug product development by Nathalie Clément, Sadik H. Kassim, Daniel Leblanc, Katy Spink, John Tomtishen
Published 2024-03-01
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NaCl and KCl mediate log increase in AAV vector particles and infectious titers in a specific/timely manner with the HSV platform by Chenghui Yu, Prasad D. Trivedi, Payel Chaudhuri, Radhika Bhake, Evan J. Johnson, Tina Caton, Mark Potter, Barry J. Byrne, Nathalie Clément
Published 2021-06-01
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Comparison of highly pure rAAV9 vector stocks produced in suspension by PEI transfection or HSV infection reveals striking quantitative and qualitative differences by Prasad D. Trivedi, Chenghui Yu, Payel Chaudhuri, Evan J. Johnson, Tina Caton, Laura Adamson, Barry J. Byrne, Nicole K. Paulk, Nathalie Clément
Published 2022-03-01
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Comparative impact of AAV and enzyme replacement therapy on respiratory and cardiac function in adult Pompe mice by Darin J Falk, Meghan S Soustek, Adrian Gary Todd, Cathryn S Mah, Denise A Cloutier, Jeffry S Kelley, Nathalie Clement, David D Fuller, Barry J Byrne
Published 2015-01-01
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A simplified purification protocol for recombinant adeno-associated virus vectors by Mark Potter, Bridget Lins, Mario Mietzsch, Regine Heilbronn, Kim Van Vliet, Paul Chipman, Mavis Agbandje-McKenna, Brian D Cleaver, Nathalie Clément, Barry J Byrne, Sergei Zolotukhin
Published 2014-01-01
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Micro-dystrophin AAV Vectors Made by Transient Transfection and Herpesvirus System Are Equally Potent in Treating mdx Mouse Muscle Disease by Chady H. Hakim, Nathalie Clément, Lakmini P. Wasala, Hsiao T. Yang, Yongping Yue, Keqing Zhang, Kasun Kodippili, Laura Adamson-Small, Xiufang Pan, Joel S. Schneider, N. Nora Yang, Jeffrey S. Chamberlain, Barry J. Byrne, Dongsheng Duan
Published 2020-09-01
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Seroprevalence of anti-SARS-CoV-2 IgG at the first epidemic peak in French Guiana, July 2020. by Claude Flamand, Christelle Alves Sarmento, Antoine Enfissi, Sarah Bailly, Emmanuel Beillard, Mélanie Gaillet, Céline Michaud, Véronique Servas, Nathalie Clement, Anaïs Perilhou, Thierry Carage, Didier Musso, Jean-François Carod, Stéphanie Eustache, Céline Tourbillon, Elodie Boizon, Samantha James, Félix Djossou, Henrik Salje, Simon Cauchemez, Dominique Rousset
Published 2021-11-01
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Adeno-associated virus-mediated gene therapy in a patient with Canavan disease using dual routes of administration and immune modulation by Manuela Corti, Barry J. Byrne, Dominic J. Gessler, Grace Thompson, Samantha Norman, Jenna Lammers, Kirsten E. Coleman, Cristina Liberati, Melissa E. Elder, Maria L. Escolar, Ibrahim S. Tuna, Clementina Mesaros, Gary I. Kleiner, Deborah S. Barbouth, Heather L. Gray-Edwards, Nathalie Clement, Brian D. Cleaver, Guangping Gao
Published 2023-09-01
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Identification of pathway-biased and deleterious melatonin receptor mutants in autism spectrum disorders and in the general population. by Pauline Chaste, Nathalie Clement, Oriane Mercati, Jean-Luc Guillaume, Richard Delorme, Hany Goubran Botros, Cécile Pagan, Samuel Périvier, Isabelle Scheid, Gudrun Nygren, Henrik Anckarsäter, Maria Rastam, Ola Ståhlberg, Carina Gillberg, Emilie Serrano, Nathalie Lemière, Jean Marie Launay, Marie Christine Mouren-Simeoni, Marion Leboyer, Christopher Gillberg, Ralf Jockers, Thomas Bourgeron
Published 2010-07-01
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The orphan GPR50 receptor promotes constitutive TGFβ receptor signaling and protects against cancer development by Stefanie Wojciech, Raise Ahmad, Zakia Belaid-Choucair, Anne-Sophie Journé, Sarah Gallet, Julie Dam, Avais Daulat, Delphine Ndiaye-Lobry, Olivier Lahuna, Angeliki Karamitri, Jean-Luc Guillaume, Marcio Do Cruzeiro, François Guillonneau, Anastasia Saade, Nathalie Clément, Thomas Courivaud, Nawel Kaabi, Kenjiro Tadagaki, Philippe Delagrange, Vincent Prévot, Olivier Hermine, Céline Prunier, Ralf Jockers
Published 2018-03-01
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