Hasil Pencarian - Leszek Lisowski
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1
The future of recombinant host defense peptides oleh Ramon Roca-Pinilla, Leszek Lisowski, Anna Arís, Elena Garcia-Fruitós
Diterbitkan 2022-12-01Dapatkan teks lengkap
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2
The intersection of vector biology, gene therapy, and hemophilia oleh Leszek Lisowski, Janice M. Staber, J. Fraser Wright, Leonard A. Valentino
Diterbitkan 2021-08-01Dapatkan teks lengkap
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3
Alzheimer’s disease induced neurons bearing PSEN1 mutations exhibit reduced excitability oleh Simon Maksour, Rocio K. Finol-Urdaneta, Amy J. Hulme, Mauricio e Castro Cabral-da-Silva, Helena Targa Dias Anastacio, Rachelle Balez, Tracey Berg, Calista Turner, Sonia Sanz Muñoz, Martin Engel, Predrag Kalajdzic, Leszek Lisowski, Leszek Lisowski, Leszek Lisowski, Kuldip Sidhu, Perminder S. Sachdev, Mirella Dottori, Lezanne Ooi
Diterbitkan 2024-10-01Dapatkan teks lengkap
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5
Neurological Disorders Associated with WWOX Germline Mutations—A Comprehensive Overview oleh Ehud Banne, Baraa Abudiab, Sara Abu-Swai, Srinivasa Rao Repudi, Daniel J. Steinberg, Diala Shatleh, Sarah Alshammery, Leszek Lisowski, Wendy Gold, Peter L. Carlen, Rami I. Aqeilan
Diterbitkan 2021-04-01Dapatkan teks lengkap
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6
Safety and efficacy of an engineered hepatotropic AAV gene therapy for ornithine transcarbamylase deficiency in cynomolgus monkeys oleh Julien Baruteau, Sharon C. Cunningham, Berna Seker Yilmaz, Dany P. Perocheau, Simon Eaglestone, Derek Burke, Adrian J. Thrasher, Simon N. Waddington, Leszek Lisowski, Ian E. Alexander, Paul Gissen
Diterbitkan 2021-12-01Dapatkan teks lengkap
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7
Engineering domain-inlaid SaCas9 adenine base editors with reduced RNA off-targets and increased on-target DNA editing oleh Minh Thuan Nguyen Tran, Mohd Khairul Nizam Mohd Khalid, Qi Wang, Jacqueline K. R. Walker, Grace E. Lidgerwood, Kimberley L. Dilworth, Leszek Lisowski, Alice Pébay, Alex W. Hewitt
Diterbitkan 2020-09-01Dapatkan teks lengkap
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8
ADEVO: Proof-of-concept of adenovirus-directed EVOlution by random peptide display on the fiber knob oleh Erwan Sallard, Julian Fischer, Katrin Schroeer, Lisa-Marie Dawson, Nissai Beaude, Arsalene Affes, Eric Ehrke-Schulz, Wenli Zhang, Adrian Westhaus, Marti Cabanes-Creus, Leszek Lisowski, Zsolt Ruszics, Anja Ehrhardt
Diterbitkan 2024-12-01Dapatkan teks lengkap
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9
Single amino acid insertion allows functional transduction of murine hepatocytes with human liver tropic AAV capsids oleh Marti Cabanes-Creus, Renina Gale Navarro, Sophia H.Y. Liao, Grober Baltazar, Matthieu Drouyer, Erhua Zhu, Suzanne Scott, Clement Luong, Laurence O.W. Wilson, Ian E. Alexander, Leszek Lisowski
Diterbitkan 2021-06-01Dapatkan teks lengkap
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10
AAVolve: Concatenated long-read deep sequencing enables whole capsid tracking during shuffled AAV library selection oleh Suzanne Scott, Adrian Westhaus, Deborah Nazareth, Marti Cabanes-Creus, Renina Gale Navarro, Deborah Chandra, Erhua Zhu, Aravind Venkateswaran, Ian E. Alexander, Denis C. Bauer, Laurence O.W. Wilson, Leszek Lisowski
Diterbitkan 2024-12-01Dapatkan teks lengkap
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11
Multiplexed in vivo homology-directed repair and tumor barcoding enables parallel quantification of Kras variant oncogenicity oleh Ian P. Winters, Shin-Heng Chiou, Nicole K. Paulk, Christopher D. McFarland, Pranav V. Lalgudi, Rosanna K. Ma, Leszek Lisowski, Andrew J. Connolly, Dmitri A. Petrov, Mark A. Kay, Monte M. Winslow
Diterbitkan 2017-12-01Dapatkan teks lengkap
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12
A hepatic network of dendritic cells mediates CD4 T cell help outside lymphoid organs oleh Kieran English, Rain Kwan, Lauren E. Holz, Claire McGuffog, Jelte M. M. Krol, Daryan Kempe, Tsuneyasu Kaisho, William R. Heath, Leszek Lisowski, Maté Biro, Geoffrey W. McCaughan, David G. Bowen, Patrick Bertolino
Diterbitkan 2024-02-01Dapatkan teks lengkap
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13
Optogenetic restoration of high sensitivity vision with bReaChES, a red-shifted channelrhodopsin oleh Lay Khoon Too, Weiyong Shen, Dario A. Protti, Atomu Sawatari, Dylan A. Black, Catherine A. Leamey, Jin Y. Huang, So-Ra Lee, Ashish E. Mathai, Leszek Lisowski, John Y. Lin, Mark C. Gillies, Matthew P. Simunovic
Diterbitkan 2022-11-01Dapatkan teks lengkap
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14
Long-term ex situ normothermic perfusion of human split livers for more than 1 week oleh Ngee-Soon Lau, Mark Ly, Claude Dennis, Andrew Jacques, Marti Cabanes-Creus, Shamus Toomath, Joanna Huang, Nicole Mestrovic, Paul Yousif, Sumon Chanda, Chuanmin Wang, Leszek Lisowski, Ken Liu, James G. Kench, Geoffrey McCaughan, Michael Crawford, Carlo Pulitano
Diterbitkan 2023-08-01Dapatkan teks lengkap
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15
Bioengineered Viral Platform for Intramuscular Passive Vaccine Delivery to Human Skeletal Muscle oleh Nicole K. Paulk, Katja Pekrun, Gregory W. Charville, Katie Maguire-Nguyen, Michael N. Wosczyna, Jianpeng Xu, Yue Zhang, Leszek Lisowski, Bryan Yoo, Jose G. Vilches-Moure, Gordon K. Lee, Joseph B. Shrager, Thomas A. Rando, Mark A. Kay
Diterbitkan 2018-09-01Dapatkan teks lengkap
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16
Novel AAV variants with improved tropism for human Schwann cells oleh Matthieu Drouyer, Tak-Ho Chu, Elodie Labit, Florencia Haase, Renina Gale Navarro, Deborah Nazareth, Nicole Rosin, Jessica Merjane, Suzanne Scott, Marti Cabanes-Creus, Adrian Westhaus, Erhua Zhu, Rajiv Midha, Ian E. Alexander, Jeff Biernaskie, Samantha L. Ginn, Leszek Lisowski
Diterbitkan 2024-06-01Dapatkan teks lengkap
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17
Characterization of the humanized FRG mouse model and development of an AAV-LK03 variant with improved liver lobular biodistribution oleh Marti Cabanes-Creus, Renina Gale Navarro, Sophia H.Y. Liao, Suzanne Scott, Rodrigo Carlessi, Ramon Roca-Pinilla, Maddison Knight, Grober Baltazar, Erhua Zhu, Matthew Jones, Elena Denisenko, Alistair R.R. Forrest, Ian E. Alexander, Janina E.E. Tirnitz-Parker, Leszek Lisowski
Diterbitkan 2023-03-01Dapatkan teks lengkap
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18
Novel human liver-tropic AAV variants define transferable domains that markedly enhance the human tropism of AAV7 and AAV8 oleh Marti Cabanes-Creus, Renina Gale Navarro, Erhua Zhu, Grober Baltazar, Sophia H.Y. Liao, Matthieu Drouyer, Anais K. Amaya, Suzanne Scott, Loan Hanh Nguyen, Adrian Westhaus, Matthias Hebben, Laurence O.W. Wilson, Adrian J. Thrasher, Ian E. Alexander, Leszek Lisowski
Diterbitkan 2022-03-01Dapatkan teks lengkap
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19
Efficient in vivo editing of OTC-deficient patient-derived primary human hepatocytes oleh Samantha L. Ginn, Anais K. Amaya, Sophia H.Y. Liao, Erhua Zhu, Sharon C. Cunningham, Michael Lee, Claus V. Hallwirth, Grant J. Logan, Szun S. Tay, Anthony J. Cesare, Hilda A. Pickett, Markus Grompe, Kimberley Dilworth, Leszek Lisowski, Ian E. Alexander
Diterbitkan 2020-02-01Dapatkan teks lengkap
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20
AAV capsid bioengineering in primary human retina models oleh Adrian Westhaus, Steven S. Eamegdool, Milan Fernando, Paula Fuller-Carter, Alicia A. Brunet, Annie L. Miller, Rabab Rashwan, Maddison Knight, Maciej Daniszewski, Grace E. Lidgerwood, Alice Pébay, Alex Hewitt, Giorgia Santilli, Adrian J. Thrasher, Livia S. Carvalho, Anai Gonzalez-Cordero, Robyn V. Jamieson, Leszek Lisowski
Diterbitkan 2023-12-01Dapatkan teks lengkap
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