Hasil Pencarian - Jean Mercer
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Home infusion with Elosulfase alpha (VimizimR) in a UK Paediatric setting oleh Niamh Finnigan, Jane Roberts, Jean Mercer, Simon A. Jones
Diterbitkan 2018-03-01Dapatkan teks lengkap
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Toward a Core Outcome Set for Head, Neck, and Respiratory Disease in Mucopolysaccharidosis Type II: Systematic Literature Review and Assessment of Heterogeneity in Outcome Reportin... oleh Aleksandra Metryka, Nailah Brown, Jean Mercer, Stuart Wilkinson, Simon Jones, Paula Williamson, Iain Bruce
Diterbitkan 2019-04-01Dapatkan teks lengkap
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Impact of long-term elosulfase alfa treatment on clinical and patient-reported outcomes in patients with mucopolysaccharidosis type IVA: results from a Managed Access Agreement in... oleh Maureen Cleary, James Davison, Rachel Gould, Tarekegn Geberhiwot, Derralynn Hughes, Jean Mercer, Alexandra Morrison, Elaine Murphy, Saikat Santra, James Jarrett, Swati Mukherjee, Karolina M. Stepien
Diterbitkan 2021-01-01Dapatkan teks lengkap
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Hematopoietic stem cell transplantation improves the high incidence of neutralizing allo-antibodies observed in Hurler’s syndrome after pharmacological enzyme replacement therapy oleh Muhammad Ameer Saif, Brian W. Bigger, Karen E Brookes, Jean Mercer, Karen L. Tylee, Heather J. Church, Denise K. Bonney, Simon Jones, J. Ed Wraith, Robert F. Wynn
Diterbitkan 2012-09-01Dapatkan teks lengkap
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