Hasil Pencarian - Frank Rigo
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Manipulation of PK-M mutually exclusive alternative splicing by antisense oligonucleotides oleh Zhenxun Wang, Hyun Yong Jeon, Frank Rigo, C. Frank Bennett, Adrian R. Krainer
Diterbitkan 2012-01-01Dapatkan teks lengkap
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Knockdown of GADD34 in neonatal mutant SOD1 mice ameliorates ALS oleh Ghanashyam D. Ghadge, Yoshifumi Sonobe, Adrian Camarena, Claire Drigotas, Frank Rigo, Karen K. Ling, Raymond P. Roos
Diterbitkan 2020-03-01Dapatkan teks lengkap
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Long-Term <i>SMN</i>- and <i>Ncald</i>-ASO Combinatorial Therapy in SMA Mice and <i>NCALD</i>-ASO Treatment in hiPSC-Derived Motor Neurons Show Protective Effects oleh Anixa Muiños-Bühl, Roman Rombo, Karen K. Ling, Eleonora Zilio, Frank Rigo, C. Frank Bennett, Brunhilde Wirth
Diterbitkan 2023-02-01Dapatkan teks lengkap
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PHAROH lncRNA regulates Myc translation in hepatocellular carcinoma via sequestering TIAR oleh Allen T Yu, Carmen Berasain, Sonam Bhatia, Keith Rivera, Bodu Liu, Frank Rigo, Darryl J Pappin, David L Spector
Diterbitkan 2021-05-01Dapatkan teks lengkap
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Antisense-mediated reduction of EphA4 in the adult CNS does not improve the function of mice with amyotrophic lateral sclerosis oleh Karen K. Ling, Michaela Jackson, Duah Alkam, Dawei Liu, Norm Allaire, Chao Sun, Mahmoud Kiaei, Alexander McCampbell, Frank Rigo
Diterbitkan 2018-06-01Dapatkan teks lengkap
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Non-invasive monitoring of alternative splicing outcomes to identify candidate therapies for myotonic dystrophy type 1 oleh Ningyan Hu, Layal Antoury, Timothy M. Baran, Soumya Mitra, C. Frank Bennett, Frank Rigo, Thomas H. Foster, Thurman M. Wheeler
Diterbitkan 2018-12-01Dapatkan teks lengkap
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Targeting nonsense-mediated RNA decay does not increase progranulin levels in the Grn R493X mouse model of frontotemporal dementia. oleh Denise M Smith, Michael L Niehoff, Karen Ling, Paymaan Jafar-Nejad, Frank Rigo, Susan A Farr, Miles F Wilkinson, Andrew D Nguyen
Diterbitkan 2023-01-01Dapatkan teks lengkap
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Targeting nonsense-mediated RNA decay does not increase progranulin levels in the GrnR493X mouse model of frontotemporal dementia oleh Denise M. Smith, Michael L. Niehoff, Karen Ling, Paymaan Jafar-Nejad, Frank Rigo, Susan A. Farr, Miles F. Wilkinson, Andrew D. Nguyen
Diterbitkan 2023-01-01Dapatkan teks lengkap
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Disrupted neuronal maturation in Angelman syndrome-derived induced pluripotent stem cells oleh James J. Fink, Tiwanna M. Robinson, Noelle D. Germain, Carissa L. Sirois, Kaitlyn A. Bolduc, Amanda J. Ward, Frank Rigo, Stormy J. Chamberlain, Eric S. Levine
Diterbitkan 2017-04-01Dapatkan teks lengkap
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Antisense Oligonucleotide-Mediated Reduction of HDAC6 Does Not Reduce Tau Pathology in P301S Tau Transgenic Mice oleh Antonio Valencia, Veronica L. Reinhart Bieber, Bekim Bajrami, Galina Marsh, Stefan Hamann, Ru Wei, Karen Ling, Frank Rigo, H. Moore Arnold, Olga Golonzhka, Heike Hering
Diterbitkan 2021-06-01Dapatkan teks lengkap
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Astrocytic 4R tau expression drives astrocyte reactivity and dysfunction oleh Lubov A. Ezerskiy, Kathleen M. Schoch, Chihiro Sato, Mariana Beltcheva, Kanta Horie, Frank Rigo, Ryan Martynowicz, Celeste M. Karch, Randall J. Bateman, Timothy M. Miller
Diterbitkan 2022-01-01Dapatkan teks lengkap
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Splice-switching of the insulin receptor pre-mRNA alleviates tumorigenic hallmarks in rhabdomyosarcoma oleh Safiya Khurshid, Matias Montes, Daniel F. Comiskey, Brianne Shane, Eleftheria Matsa, Francesca Jung, Chelsea Brown, Hemant Kumar Bid, Ruoning Wang, Peter J. Houghton, Ryan Roberts, Frank Rigo, Dawn Chandler
Diterbitkan 2022-01-01Dapatkan teks lengkap
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Systemic delivery of a DUX4-targeting antisense oligonucleotide to treat facioscapulohumeral muscular dystrophy oleh Linde F. Bouwman, Bianca den Hamer, Anita van den Heuvel, Marnix Franken, Michaela Jackson, Chrissa A. Dwyer, Stephen J. Tapscott, Frank Rigo, Silvère M. van der Maarel, Jessica C. de Greef
Diterbitkan 2021-12-01Dapatkan teks lengkap
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Reduction of matrix metalloproteinase 9 (MMP-9) protects motor neurons from TDP-43-triggered death in rNLS8 mice oleh Krista J. Spiller, Tahiyana Khan, Myrna A. Dominique, Clark R. Restrepo, Dejania Cotton-Samuel, Maya Levitan, Paymaan Jafar-Nejad, Bin Zhang, Armand Soriano, Frank Rigo, John Q. Trojanowski, Virginia M.-Y. Lee
Diterbitkan 2019-04-01Dapatkan teks lengkap
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