Hasil Pencarian - Donald B Kohn
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Improved SARS-CoV-2 Spike Glycoproteins for Pseudotyping Lentiviral Vectors oleh Paul G. Ayoub, Arunima Purkayastha, Jason Quintos, Curtis Tam, Lindsay Lathrop, Kevin Tam, Marlene Ruiz, Roger P. Hollis, Brigitte N. Gomperts, Brigitte N. Gomperts, Brigitte N. Gomperts, Donald B. Kohn, Donald B. Kohn, Donald B. Kohn, Donald B. Kohn, Donald B. Kohn
Diterbitkan 2021-11-01Dapatkan teks lengkap
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Gene Therapies for Primary Immune Deficiencies oleh Lisa A. Kohn, Donald B. Kohn
Diterbitkan 2021-02-01Dapatkan teks lengkap
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Improved lentiviral vector titers from a multi-gene knockout packaging line oleh Jiaying Han, Kevin Tam, Curtis Tam, Roger P. Hollis, Donald B. Kohn
Diterbitkan 2021-12-01Dapatkan teks lengkap
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Gene delivery using AAV8 in vivo for disease stabilization in a bimodal gene therapy approach for the treatment of ADA-deficient SCID oleh Denise A. Carbonaro-Sarracino, Krista Chun, Danielle N. Clark, Michael L. Kaufman, Xiangyang Jin, Xiaoyan Wang, Donald B. Kohn
Diterbitkan 2021-03-01Dapatkan teks lengkap
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Pre-clinical Development of a Lentiviral Vector Expressing the Anti-sickling βAS3 Globin for Gene Therapy for Sickle Cell Disease oleh Valentina Poletti, Fabrizia Urbinati, Sabine Charrier, Guillaume Corre, Roger P. Hollis, Beatriz Campo Fernandez, Samia Martin, Michael Rothe, Axel Schambach, Donald B. Kohn, Fulvio Mavilio
Diterbitkan 2018-12-01Dapatkan teks lengkap
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Reactivating Fetal Hemoglobin Expression in Human Adult Erythroblasts Through BCL11A Knockdown Using Targeted Endonucleases oleh Carmen F Bjurström, Michelle Mojadidi, John Phillips, Caroline Kuo, Stephen Lai, Georgia R Lill, Aaron Cooper, Michael Kaufman, Fabrizia Urbinati, Xiaoyan Wang, Roger P Hollis, Donald B Kohn
Diterbitkan 2016-01-01Dapatkan teks lengkap
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Domain-swapped T cell receptors improve the safety of TCR gene therapy oleh Michael T Bethune, Marvin H Gee, Mario Bunse, Mark S Lee, Eric H Gschweng, Meghana S Pagadala, Jing Zhou, Donghui Cheng, James R Heath, Donald B Kohn, Michael S Kuhns, Wolfgang Uckert, David Baltimore
Diterbitkan 2016-11-01Dapatkan teks lengkap
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Human CLEC9A antibodies deliver NY-ESO-1 antigen to CD141+ dendritic cells to activate naïve and memory NY-ESO-1-specific CD8+ T cells oleh Oscar L Haigh, Kirsteen M Tullett, Carina Walpole, Jonathon Cebon, Christopher Schmidt, Liam O'Brien, Nikita Rosendahl, Ghazal Daraj, Irina Caminschi, Eric H Gschweng, Roger P Hollis, Donald B Kohn, Mireille H Lahoud
Diterbitkan 2020-07-01Dapatkan teks lengkap
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The human ankyrin 1 promoter insulator sustains gene expression in a β-globin lentiviral vector in hematopoietic stem cells oleh Zulema Romero, Beatriz Campo-Fernandez, Jennifer Wherley, Michael L Kaufman, Fabrizia Urbinati, Aaron R Cooper, Megan D Hoban, Kismet M Baldwin, Dianne Lumaquin, Xiaoyan Wang, Shantha Senadheera, Roger P Hollis, Donald B Kohn
Diterbitkan 2015-01-01Dapatkan teks lengkap
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Dosing and Re-Administration of Lentiviral Vector for In Vivo Gene Therapy in Rhesus Monkeys and ADA-Deficient Mice oleh Denise A. Carbonaro-Sarracino, Alice F. Tarantal, C. Chang I. Lee, Michael L. Kaufman, Stephen Wandro, Xiangyang Jin, Michele Martinez, Danielle N. Clark, Krista Chun, Colin Koziol, Cinnamon L. Hardee, Xiaoyan Wang, Donald B. Kohn
Diterbitkan 2020-03-01Dapatkan teks lengkap
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Creating New β-Globin-Expressing Lentiviral Vectors by High-Resolution Mapping of Locus Control Region Enhancer Sequences oleh Richard A. Morgan, Feiyang Ma, Mildred J. Unti, Devin Brown, Paul George Ayoub, Curtis Tam, Lindsay Lathrop, Bamidele Aleshe, Ryo Kurita, Yukio Nakamura, Shantha Senadheera, Ryan L. Wong, Roger P. Hollis, Matteo Pellegrini, Donald B. Kohn
Diterbitkan 2020-06-01Dapatkan teks lengkap
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Global and Local Manipulation of DNA Repair Mechanisms to Alter Site-Specific Gene Editing Outcomes in Hematopoietic Stem Cells oleh Elizabeth K. Benitez, Anastasia Lomova Kaufman, Lilibeth Cervantes, Danielle N. Clark, Paul G. Ayoub, Shantha Senadheera, Kyle Osborne, Julie M. Sanchez, Ralph Valentine Crisostomo, Xiaoyan Wang, Nina Reuven, Yosef Shaul, Roger P. Hollis, Zulema Romero, Donald B. Kohn
Diterbitkan 2020-12-01Dapatkan teks lengkap
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Differentiation of RPE cells from integration-free iPS cells and their cell biological characterization oleh Roni A. Hazim, Saravanan Karumbayaram, Mei Jiang, Anupama Dimashkie, Vanda S. Lopes, Douran Li, Barry L. Burgess, Preethi Vijayaraj, Jackelyn A. Alva-Ornelas, Jerome A. Zack, Donald B. Kohn, Brigitte N. Gomperts, April D. Pyle, William E. Lowry, David S. Williams
Diterbitkan 2017-10-01Dapatkan teks lengkap
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Correction to: Differentiation of RPE cells from integration-free iPS cells and their cell biological characterization oleh Roni A. Hazim, Saravanan Karumbayaram, Mei Jiang, Anupama Dimashkie, Vanda S. Lopes, Douran Li, Barry L. Burgess, Preethi Vijayaraj, Jackelyn A. Alva-Ornelas, Jerome A. Zack, Donald B. Kohn, Brigitte N. Gomperts, April D. Pyle, William E. Lowry, David S. Williams
Diterbitkan 2019-02-01Dapatkan teks lengkap
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Site-Specific Gene Editing of Human Hematopoietic Stem Cells for X-Linked Hyper-IgM Syndrome oleh Caroline Y. Kuo, Joseph D. Long, Beatriz Campo-Fernandez, Satiro de Oliveira, Aaron R. Cooper, Zulema Romero, Megan D. Hoban, Alok V. Joglekar, Georgia R. Lill, Michael L. Kaufman, Sorel Fitz-Gibbon, Xiaoyan Wang, Roger P. Hollis, Donald B. Kohn
Diterbitkan 2018-05-01Dapatkan teks lengkap
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Lentiviral vectors for precise expression to treat X-linked lymphoproliferative disease oleh Paul G. Ayoub, Julia Gensheimer, Lindsay Lathrop, Colin Juett, Jason Quintos, Kevin Tam, Jack Reid, Feiyang Ma, Curtis Tam, Grace E. McAuley, Devin Brown, Xiaomeng Wu, Ruixue Zhang, Kathryn Bradford, Roger P. Hollis, Gay M. Crooks, Donald B. Kohn
Diterbitkan 2024-12-01Dapatkan teks lengkap
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T cell dynamics and response of the microbiota after gene therapy to treat X-linked severe combined immunodeficiency oleh Erik L. Clarke, A. Jesse Connell, Emmanuelle Six, Nadia A. Kadry, Arwa A. Abbas, Young Hwang, John K. Everett, Casey E. Hofstaedter, Rebecca Marsh, Myriam Armant, Judith Kelsen, Luigi D. Notarangelo, Ronald G. Collman, Salima Hacein-Bey-Abina, Donald B. Kohn, Marina Cavazzana, Alain Fischer, David A. Williams, Sung-Yun Pai, Frederic D. Bushman
Diterbitkan 2018-09-01Dapatkan teks lengkap
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