Hasil Pencarian - Dhanarajan Rajakumar
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Systemic delivery of an AAV9 exon-skipping vector significantly improves or prevents features of Duchenne muscular dystrophy in the Dup2 mouse oleh Nicolas Wein, Tatyana A. Vetter, Adeline Vulin, Tabatha R. Simmons, Emma C. Frair, Adrienne J. Bradley, Liubov V. Gushchina, Camila F. Almeida, Nianyuan Huang, Daniel Lesman, Dhanarajan Rajakumar, Robert B. Weiss, Kevin M. Flanigan
Diterbitkan 2022-09-01
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2
Promising AAV.U7snRNAs vectors targeting DMPK improve DM1 hallmarks in patient-derived cell lines oleh Camila F. Almeida, Florence Robriquet, Tatyana A. Vetter, Nianyuan Huang, Reid Neinast, Lumariz Hernandez-Rosario, Dhanarajan Rajakumar, W. David Arnold, W. David Arnold, Kim L. McBride, Kim L. McBride, Kevin M. Flanigan, Kevin M. Flanigan, Kevin M. Flanigan, Robert B. Weiss, Nicolas Wein, Nicolas Wein
Diterbitkan 2023-06-01
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