Hasil Pencarian - Andrew E. Mulberg
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Use of the patient-reported outcomes measurement information system (PROMISĀ®) to assess late-onset Pompe disease severity oleh Melodi Harfouche, Priya S. Kishnani, Eva Krusinska, Jamie Gault, Sheela Sitaraman, Amanda Sowinski, Irina Katz, Stephanie Austin, Margi Goldstein, Andrew E. Mulberg
Diterbitkan 2020-10-01Dapatkan teks lengkap
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Regulatory strategies for rare diseases under current global regulatory statutes: a discussion with stakeholders oleh Andrew E. Mulberg, Christina Bucci-Rechtweg, Joseph Giuliano, David Jacoby, Franklin K. Johnson, Qing Liu, Deborah Marsden, Scott McGoohan, Robert Nelson, Nita Patel, Klaus Romero, Vikram Sinha, Sheela Sitaraman, John Spaltro, Vivian Kessler
Diterbitkan 2019-02-01Dapatkan teks lengkap
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